Clik here to view.
One-Time, Lasting Treatment for Sickle Cell Disease May be on Horizon,...
For the nearly 1,000 babies born each year in the United States with sickle cell disease, a painful and arduous road awaits them. The only cure is to find a bone marrow donor—an exceedingly rare...
View ArticleClik here to view.
Gene Therapy Beats Half-Matched Stem Cell Transplant in Side-by-Side...
If you are born with Severe Combined Immunodeficiency (SCID), your childhood is anything but normal. You don’t get to play with other kids, or be held by your parents. You can’t even breathe the same...
View ArticleClik here to view.
Cell mate: the man who makes stem cells for clinical trials
When we announced that one of the researchers we fund – Dr. Henry Klassen at the University of California, Irvine – has begun his clinical trial to treat the vision-destroying disease retinitis...
View ArticleClik here to view.
HIV/AIDS: Progress and Promise of Stem Cell Research
Our friends at Americans for Cures and Youreka Science have done it again. They’ve produced another whiteboard video about the progress and promise of stem cell research that’s so inspiring that it...
View ArticleClik here to view.
While You Were Away: Gene Editing Treats Mice with Duchenne Muscular Dystrophy
Welcome back everyone! I hope you enjoyed your holiday and are looking forward to an exciting new year. My favorite thing about coming back from vacation is to see what cool new science was published....
View ArticleClik here to view.
What Went Down at ARM’s Regenerative Medicine State of the Industry
Every January, downtown San Francisco is taken over by a flock of investors, bankers, biotech companies, and scientists attending the annual JP Morgan Healthcare Conference. This meeting looks at the...
View ArticleClik here to view.
Key Steps Along the Way To Finding Treatments for HIV on World AIDS Day
Today, December 1st, is World AIDS Day. It’s a day to acknowledge the progress that is being made in HIV prevention and treatment around the world but also to renew our commitment to a future free of...
View ArticleClik here to view.
Stem cell and gene therapy research gets a good report card from industry leader
Panel discussion at ARM State of the industry briefing: left to Right Robert Preti, Chair ARM; Jeff Walsh, bluebird bio; Manfred Rudiger, Kiadis Pharma; Barbara Sasu, Pfizer; Thomas Farrell, Bellicum...
View ArticleClik here to view.
Bye Bye bubble baby disease: promising results from stem cell gene therapy...
Evangelina Padilla-Vaccaro(Front cover of CIRM’s 2016 Annual Report) You don’t need to analyze any data to know for yourself that Evangelina Vaccaro’s experimental stem cell therapy has cured her of a...
View ArticleClik here to view.
Recap of the 2018 Alliance for Regenerative Medicine Cell and Gene Therapy...
What happened in the Cell and Gene Therapy sector in 2017, and what should we be looking out for in 2018? Over 500 executives, investors, scientists and patient advocates gathered together yesterday to...
View ArticleClik here to view.
Stem Cell Round: Improving memory, building up “good” fat, nanomedicine
Stem Cell Photo of the Week In honor of brain awareness week, our featured stem cell photo is of the brain! Scientists at the Massachusetts General Hospital and Harvard Stem Cell Institute identified a...
View ArticleClik here to view.
Gene therapy and blood stem cells cure sickle cell disease patients
Sickle-shaped blood cells. The cells become lodged in blood vessels, causing strokes or excruciating pain as blood stops flowing. Photo courtesy of Omikron/Science Source Blood is the lifeline of the...
View ArticleClik here to view.
Gene therapy gives patient a cure and a new lease on life
Brenden Whittaker (left), of Ohio, is a patient born with a rare genetic immune disease who was treated at the Dana-Farber/Boston Children’s Cancer and Blood Disorders Center in a CIRM funded gene...
View ArticleClik here to view.
Promising start to CIRM-funded trial for life-threatening blood disorder
Aristotle At CIRM we are always happy to highlight success stories, particularly when they involve research we are funding. But we are also mindful of the need not to overstate a finding. To quote the...
View ArticleClik here to view.
CIRM Board Approves Funding for New Clinical Trials in Solid Tumors and...
Dr. Theodore Nowicki, physician in the division of pediatric hematology/oncology at UCLA. Photo courtesy of Milo Mitchell/UCLA Jonsson Comprehensive Cancer Center The governing Board of the California...
View ArticleClik here to view.
CIRM Board Approves New Clinical Trial for Rare Childhood Disease
Today the governing Board of the California Institute for Regenerative Medicine (CIRM) approved a grant of almost $12 million to Dr. Stephanie Cherqui at the University of California, San Diego (UCSD)...
View ArticleClik here to view.
NIH collaboration aims to develop affordable gene therapies for sickle cell...
Sickle cell disease (SCD) and HIV have a major burden on the health of impoverished communities all over the world. Of the 38 million people living with HIV all over the world, approximately 95%...
View ArticleClik here to view.
‘A Tornado at the Front Door, a Tsunami at the Back Door’
CIRM funds a lot of research and all of it has life-saving potential. But every once in a while you come across a story about someone benefiting from CIRM-supported research that highlights why the...
View ArticleClik here to view.
Scientists Engineer Stem Cells to Fight HIV
Image of the virus that causes AIDS – courtesy NIH If that headline seems familiar it should. It came from an article in MIT Technology Review back in 2009. There have been many other headlines since...
View ArticleClik here to view.
CIRM-Funded Clinical Trial for Sickle Cell Gives Hope to People Battling the...
Marissa Cors (right) with her mother Adrienne Shapiro Marissa Cors has lived with Sickle Cell Disease (SCD) for more than 40 years. The co-founder of The Sickle Cell Experience Live, an online...
View Article